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LT - COMPOSITIONS AND METHODS FOR TREATMENT OF PEROXISOMAL DISORDERS AND LEUKODYSTROPHIES
EN - COMPOSITIONS AND METHODS FOR TREATMENT OF PEROXISOMAL DISORDERS AND LEUKODYSTROPHIES

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Patent in force

Bibliographic data
Indications of the International Patent Classification (IPC)
(51) INT.CL. A61K 47/60 (2017.01)
A61K 47/59 (2017.01)
A61K 47/50 (2017.01)
A61K 49/00 (2006.01)
A61K 31/05 (2006.01)
A61K 31/192 (2006.01)
A61K 31/195 (2006.01)
A61K 31/573 (2006.01)
A61P 43/00 (2006.01)
A61P 39/06 (2006.01)
A61P 25/00 (2006.01)
A61P 15/08 (2006.01)
A61P 3/06 (2006.01)
A61P 25/28 (2006.01)
A61P 17/18 (2006.01)
European patent
(11) Number of the document 3368088
(13) Kind of document T
(96) European patent application number 16791282.3
Date of filing the European patent application 2016-10-31
(97) Date of publication of the European application 2018-09-05
(45) Date of publication and mention of the grant of the patent 2023-06-07
(46) Date of publication of the claims translation
PCT application
(86) Number PCT/US2016/059697
Date 2016-10-31
PCT application publication
(87) Number WO 2017/075580
Date 2017-05-04
Priority applications
(30) Number Date Country code
201562248163 P 2015-10-29 US
Inventors
(72)
KANNAN, Sujatha , US
RANGARAMANUJAM, Kannan , US
ZHANG, Fan , US
FATEMI, Seyed Ali , US
TURK, Bela , AT
GOK, Ozgul , TR
Grantee
(73) The Johns Hopkins University , 3400 North Charles Street, Baltimore, MD 21218, US
Kennedy Krieger Institute, Inc. , 707 North Broadway, Baltimore, Maryland 21205, US
Title
(54) COMPOSITIONS AND METHODS FOR TREATMENT OF PEROXISOMAL DISORDERS AND LEUKODYSTROPHIES
  COMPOSITIONS AND METHODS FOR TREATMENT OF PEROXISOMAL DISORDERS AND LEUKODYSTROPHIES