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LT - METHODS AND MEANS FOR EFFICIENT SKIPPING OF EXON 45 IN DUCHENNE MUSCULAR DYSTROPHY PRE-MRNA
EN - METHODS AND MEANS FOR EFFICIENT SKIPPING OF EXON 45 IN DUCHENNE MUSCULAR DYSTROPHY PRE-MRNA

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Bibliographic data
Indications of the International Patent Classification (IPC)
(51) INT.CL. C12N 15/113
A61K 31/7105
European patent
(11) Number of the document 2344637
(13) Kind of document T
(96) European patent application number 09788160.1
Date of filing the European patent application 2009-01-13
(97) Date of publication of the European application 2011-07-20
(45) Date of publication and mention of the grant of the patent 2014-12-24
(46) Date of publication of the claims translation
PCT application
(86) Number PCT/NL2009/050006
Date 2009-01-13
PCT application publication
(87) Number WO 2010/050801
Date 2010-05-06
Priority applications
(30) Number Date Country code
PCT/NL2008/0506 2008-10-27 WO
Inventors
(72)
DE KIMPE, Josephus Johannes, NL
PLATENBURG, Gerardus Johannes, NL
VAN DEUTEKOM, Judith Christina Theodora, NL
AARTSMA-RUS, Annemieke, NL
VAN OMMEN, Garrit-Jan Boudewijn, NL
Grantee
(73) Academisch Ziekenhuis Leiden, Albinusdreef 2, 2333 ZA Leiden, NL
Prosensa Technologies B.V., J.H. Oortweg 21, 2333 CH Leiden, NL
Title
(54) METHODS AND MEANS FOR EFFICIENT SKIPPING OF EXON 45 IN DUCHENNE MUSCULAR DYSTROPHY PRE-MRNA
  METHODS AND MEANS FOR EFFICIENT SKIPPING OF EXON 45 IN DUCHENNE MUSCULAR DYSTROPHY PRE-MRNA