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LT - TREATMENT OF OCULOPHARYNGEAL MUSCULAR DYSTROPHY BY INTRAVENOUS ADMINISTRATION OF TREHALOSE
EN - TREATMENT OF OCULOPHARYNGEAL MUSCULAR DYSTROPHY BY INTRAVENOUS ADMINISTRATION OF TREHALOSE

Legal status

Patent not validated

Bibliographic data
Indications of the International Patent Classification (IPC)
(51) INT.CL. A61K 31/7016 (2006.01)
A61K 31/7016 (2013.01)
A61P 21/00 (2006.01)
A61K 9/0019 (2013.01)
A61P 25/14 (2006.01)
A61P 11/04 (2018.01)
A61P 25/16 (2006.01)
A61P 21/00 (2018.01)
A61P 25/28 (2006.01)
A61P 21/04 (2018.01)
A61K 9/00 (2006.01)
A61P 25/00 (2018.01)
A61P 25/14 (2018.01)
A61P 25/16 (2018.01)
A61P 25/28 (2018.01)
European patent
(11) Number of the document 2994145
(13) Kind of document T
(96) European patent application number 14733380.1
Date of filing the European patent application 2014-05-07
(97) Date of publication of the European application 2016-03-16
(45) Date of publication and mention of the grant of the patent 2023-01-04
(46) Date of publication of the claims translation
PCT application
(86) Number PCT/IL2014/050411
Date 2014-05-07
PCT application publication
(87) Number WO 2014/181333
Date 2014-11-13
Priority applications
(30) Number Date Country code
201361820278 P 2013-05-07 US
Inventors
(72)
MEGIDDO, Dalia , IL
Grantee
(73) Bio Blast Pharma Ltd. , 37 Menachem Begin Street Rubinstein Tower, 15th floor, 6522042 Tel Aviv, IL
Title
(54) TREATMENT OF OCULOPHARYNGEAL MUSCULAR DYSTROPHY BY INTRAVENOUS ADMINISTRATION OF TREHALOSE
  TREATMENT OF OCULOPHARYNGEAL MUSCULAR DYSTROPHY BY INTRAVENOUS ADMINISTRATION OF TREHALOSE