![]() |
![]() |
Teisinis statusas
Patentas neįsigaliojo (pagal EPK)
(51) | INT.CL. | C12N 15/113 | |
A61K 31/7088 |
(11) | Patento numeris | 3019610 |
(13) | Dokumento rūšis | T |
(96) | Europos patento paraiškos numeris | 14737236.1 |
Europos patento paraiškos padavimo data | 2014-07-08 | |
(97) | Europos patento paraiškos paskelbimo data | 2016-05-18 |
(45) | Paskelbimo apie Europos patento išdavimą data | 2020-05-06 |
(46) | Apibrėžties vertimo paskelbimo data |
(86) | Numeris | PCT/EP2014/064604 |
Data | 2014-07-08 |
(87) | Numeris | WO 2015/004133 |
Data | 2015-01-15 |
(30) | Numeris | Data | Šalis |
13305968 | 2013-07-08 | EP |
(72) |
ROZET, Jean-Michel, FR
PERRAULT, Isabelle, FR
GERARD, Xavier, FR
KAPLAN, Josseline, FR
MUNNICH, Arnold, FR
|
(73) |
INSERM (Institut National de la Santé et de la Recherche Médicale),
101, rue de Tolbiac, 75013 Paris,
FR
Assistance Publique-Hōpitaux de Paris (APHP), 3, avenue Victoria, 75004 Paris, FR Fondation Imagine, 24, Boulevard du Montparnasse, 75015 Paris, FR Université de Paris, 85 boulevard Saint Germain, 75006 Paris, FR |
(54) | METHODS FOR PERFORMING ANTISENSE OLIGONUCLEOTIDE-MEDIATED EXON SKIPPING IN THE RETINA OF A SUBJECT IN NEED THEREOF |
METHODS FOR PERFORMING ANTISENSE OLIGONUCLEOTIDE-MEDIATED EXON SKIPPING IN THE RETINA OF A SUBJECT IN NEED THEREOF |