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LT - METHODS AND MEANS FOR EFFICIENT SKIPPING OF AT LEAST EXON 52 OF THE HUMAN DUCHENNE MUSCULAR DYSTROPHY GENE
EN - METHODS AND MEANS FOR EFFICIENT SKIPPING OF AT LEAST EXON 52 OF THE HUMAN DUCHENNE MUSCULAR DYSTROPHY GENE

Legal status

Patent not validated

Bibliographic data
Indications of the International Patent Classification (IPC)
(51) INT.CL. A61K 31/711 (2006.01)
C12N 15/113 (2013.01)
A61P 21/04 (2006.01)
C12N2310/11 (2013.01)
C07J 41/00 (2006.01)
C12N2310/315 (2013.01)
C07J 1/00 (2006.01)
C12N2310/321 (2013.01)
A61K 38/17 (2006.01)
A61P 21/00 (2018.01)
A61K 31/57 (2006.01)
A61P 21/04 (2018.01)
A61K 31/56 (2006.01)
A61P 25/28 (2018.01)
A61P 25/28 (2006.01)
European patent
(11) Number of the document 3400948
(13) Kind of document T
(96) European patent application number 18180952.6
Date of filing the European patent application 2009-03-11
(97) Date of publication of the European application 2018-11-14
(45) Date of publication and mention of the grant of the patent 2022-11-02
(46) Date of publication of the claims translation
Priority applications
(30) Number Date Country code
PCT/NL2008/050673 2008-10-27 WO
Inventors
(72)
de Kimpe, Josephus Johannes , NL
Platenburg, Gerardus Johannes , NL
van Deutekom, Judith Christina Theodora , NL
Aartsma-Rus, Annemieke , NL
van Ommen, Garrit-Jan Boudewijn , NL
Grantee
(73) Academisch Ziekenhuis Leiden , Albinusdreef 2, 2333 ZA Leiden, NL
BioMarin Technologies B.V. , J.H. Oortweg 21, 2333 CH Leiden, NL
Title
(54) METHODS AND MEANS FOR EFFICIENT SKIPPING OF AT LEAST EXON 52 OF THE HUMAN DUCHENNE MUSCULAR DYSTROPHY GENE
  METHODS AND MEANS FOR EFFICIENT SKIPPING OF AT LEAST EXON 52 OF THE HUMAN DUCHENNE MUSCULAR DYSTROPHY GENE