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LT - METHODS OF TREATING FABRY DISEASE IN PATIENTS HAVING THE G9331A MUTATION IN THE GLA GENE
EN - METHODS OF TREATING FABRY DISEASE IN PATIENTS HAVING THE G9331A MUTATION IN THE GLA GENE

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Patent not validated

Bibliographic data
Indications of the International Patent Classification (IPC)
(51) INT.CL. A61K 31/445 (2006.01)
A61P 3/00 (2006.01)
European patent
(11) Number of the document 3432882
(13) Kind of document T
(96) European patent application number 17714100.9
Date of filing the European patent application 2017-03-15
(97) Date of publication of the European application 2019-01-30
(45) Date of publication and mention of the grant of the patent 2021-09-01
(46) Date of publication of the claims translation
PCT application
(86) Number PCT/US2017/022414
Date 2017-03-15
PCT application publication
(87) Number WO 2017/165164
Date 2017-09-28
Priority applications
(30) Number Date Country code
201662311511 P 2016-03-22 US
Inventors
(72)
BENJAMIN, Elfrida , US
Grantee
(73) Amicus Therapeutics, Inc. , 3675 Market Street, Philadelphia, PA 19104, US
Title
(54) METHODS OF TREATING FABRY DISEASE IN PATIENTS HAVING THE G9331A MUTATION IN THE GLA GENE
  METHODS OF TREATING FABRY DISEASE IN PATIENTS HAVING THE G9331A MUTATION IN THE GLA GENE