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LT - ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRORNA-29 AND MICRO-DYSTROPHIN TO TREAT MUSCULAR DYSTROPHY
EN - ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRORNA-29 AND MICRO-DYSTROPHIN TO TREAT MUSCULAR DYSTROPHY

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Patent not validated

Bibliographic data
Indications of the International Patent Classification (IPC)
(51) INT.CL. A61K 38/1709 (2013.01)
A61K 48/00 (2006.01)
C12N 15/11 (2006.01)
C07K 14/4708 (2013.01)
C12N 15/113 (2010.01)
C12N 15/111 (2013.01)
C12N2310/141 (2013.01)
C12N2320/31 (2013.01)
C12N2330/51 (2013.01)
C12N2750/14143 (2013.01)
C12N2800/22 (2013.01)
C12N2830/008 (2013.01)
A61K 31/7088 (2013.01)
A61K 48/0058 (2013.01)
C12N 15/86 (2013.01)
A61P 21/00 (2018.01)
A61K 38/1719 (2013.01)
A61P 19/04 (2018.01)
European patent
(11) Number of the document 3442561
(13) Kind of document T
(96) European patent application number 17783235.9
Date of filing the European patent application 2017-04-14
(97) Date of publication of the European application 2019-02-20
(45) Date of publication and mention of the grant of the patent 2024-02-14
(46) Date of publication of the claims translation
PCT application
(86) Number PCT/US2017/027635
Date 2017-04-14
PCT application publication
(87) Number WO 2017/181014
Date 2017-10-19
Priority applications
(30) Number Date Country code
201662323163 P 2016-04-15 US
201762473253 P 2017-03-17 US
Inventors
(72)
RODINO-KLAPAC, Louise , US
MENDELL, Jerry, R. , US
HELLER, Kristin, N. , US
Grantee
(73) Research Institute at Nationwide Children's Hospital , 700 Children's Drive, Room W172,, Columbus, Ohio 43205, US
Title
(54) ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRORNA-29 AND MICRO-DYSTROPHIN TO TREAT MUSCULAR DYSTROPHY
  ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRORNA-29 AND MICRO-DYSTROPHIN TO TREAT MUSCULAR DYSTROPHY