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LT - COMPOSITIONS AND METHODS FOR THE TREATMENT OF LYSOSOMAL STORAGE DISORDERS AND DISORDERS CHARACTERIZED BY LYSOSOMAL DYSFUNCTION
EN - COMPOSITIONS AND METHODS FOR THE TREATMENT OF LYSOSOMAL STORAGE DISORDERS AND DISORDERS CHARACTERIZED BY LYSOSOMAL DYSFUNCTION

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Patent not validated

Bibliographic data
Indications of the International Patent Classification (IPC)
(51) INT.CL. A61K 31/7016 (2006.01)
A61K 31/4375 (2006.01)
A61P 3/00 (2006.01)
A61P 25/28 (2006.01)
European patent
(11) Number of the document 3445451
(13) Kind of document T
(96) European patent application number 17786739.7
Date of filing the European patent application 2017-04-21
(97) Date of publication of the European application 2019-02-27
(45) Date of publication and mention of the grant of the patent 2021-08-18
(46) Date of publication of the claims translation
PCT application
(86) Number PCT/US2017/028904
Date 2017-04-21
PCT application publication
(87) Number WO 2017/185010
Date 2017-10-26
Priority applications
(30) Number Date Country code
201662325535 P 2016-04-21 US
201762475295 P 2017-03-23 US
Inventors
(72)
SARDIELLO, Marco , US
Grantee
(73) Baylor College of Medicine , One Baylor Plaza, Houston, TX 77030, US
Title
(54) COMPOSITIONS AND METHODS FOR THE TREATMENT OF LYSOSOMAL STORAGE DISORDERS AND DISORDERS CHARACTERIZED BY LYSOSOMAL DYSFUNCTION
  COMPOSITIONS AND METHODS FOR THE TREATMENT OF LYSOSOMAL STORAGE DISORDERS AND DISORDERS CHARACTERIZED BY LYSOSOMAL DYSFUNCTION