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LT - SEBELIPASE ALFA FOR USE IN LIVER FIBROSIS AND TREATING LYSOSOMAL ACID LIPASE DEFICIENCY IN PATIENTS BASED ON ISHAK FIBROSIS STAGE
EN - SEBELIPASE ALFA FOR USE IN LIVER FIBROSIS AND TREATING LYSOSOMAL ACID LIPASE DEFICIENCY IN PATIENTS BASED ON ISHAK FIBROSIS STAGE

Legal status

Patent not validated

Bibliographic data
Indications of the International Patent Classification (IPC)
(51) INT.CL. A61K 38/46 (2006.01)
A61P 1/16 (2006.01)
A61P 3/00 (2006.01)
European patent
(11) Number of the document 3518962
(13) Kind of document T
(96) European patent application number 17791485.0
Date of filing the European patent application 2017-09-28
(97) Date of publication of the European application 2019-08-07
(45) Date of publication and mention of the grant of the patent 2021-06-09
(46) Date of publication of the claims translation
PCT application
(86) Number PCT/US2017/053961
Date 2017-09-28
PCT application publication
(87) Number WO 2018/064303
Date 2018-04-05
Priority applications
(30) Number Date Country code
201662402183 P 2016-09-30 US
201662420233 P 2016-11-10 US
201762456511 P 2017-02-08 US
Inventors
(72)
QUINN, Anthony , US
GOODMAN, Zachary , US
BURTON, Barbara , US
RANKIN, Andrew , US
FRIEDMAN, Mark , US
SONI, Paresh , US
Grantee
(73) Alexion Pharmaceuticals, Inc. , 121 Seaport Boulevard, Boston, MA 02210, US
Title
(54) SEBELIPASE ALFA FOR USE IN LIVER FIBROSIS AND TREATING LYSOSOMAL ACID LIPASE DEFICIENCY IN PATIENTS BASED ON ISHAK FIBROSIS STAGE
  SEBELIPASE ALFA FOR USE IN LIVER FIBROSIS AND TREATING LYSOSOMAL ACID LIPASE DEFICIENCY IN PATIENTS BASED ON ISHAK FIBROSIS STAGE