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LT - RECOMBINANT HUMAN ACID SPHINGOMYELINASE FOR USE IN TREATING ABNORMAL BONE CONDITIONS IN ACID SPHINGOMYELINASE DEFICIENCY PATIENTS
EN - RECOMBINANT HUMAN ACID SPHINGOMYELINASE FOR USE IN TREATING ABNORMAL BONE CONDITIONS IN ACID SPHINGOMYELINASE DEFICIENCY PATIENTS

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Patent not validated

Bibliographic data
Indications of the International Patent Classification (IPC)
(51) INT.CL. A61K 38/46 (2006.01)
A61K 38/465 (2013.01)
A61P 3/00 (2006.01)
A61P 3/00 (2018.01)
A61P 19/10 (2006.01)
A61P 19/10 (2018.01)
A61P 19/08 (2006.01)
A61P 19/08 (2018.01)
European patent
(11) Number of the document 3672622
(13) Kind of document T
(96) European patent application number 18768948.4
Date of filing the European patent application 2018-08-22
(97) Date of publication of the European application 2020-07-01
(45) Date of publication and mention of the grant of the patent 2023-11-08
(46) Date of publication of the claims translation
PCT application
(86) Number PCT/IB2018/056346
Date 2018-08-22
PCT application publication
(87) Number WO 2019/038685
Date 2019-02-28
Priority applications
(30) Number Date Country code
201762549732 P 2017-08-24 US
17306720 2017-12-07 EP
Inventors
(72)
SCHEIDT-PUGA, Ana Cristina , FR
Grantee
(73) Genzyme Corporation , 450 Water Street, Cambridge, MA 02141, US
Title
(54) RECOMBINANT HUMAN ACID SPHINGOMYELINASE FOR USE IN TREATING ABNORMAL BONE CONDITIONS IN ACID SPHINGOMYELINASE DEFICIENCY PATIENTS
  RECOMBINANT HUMAN ACID SPHINGOMYELINASE FOR USE IN TREATING ABNORMAL BONE CONDITIONS IN ACID SPHINGOMYELINASE DEFICIENCY PATIENTS