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Legal status
Patent not validated
| (51) | INT.CL. | A61K 31/7105 | |
| C12N 5/10 | |||
| A61K 48/00 | |||
| A61P 21/00 |
| (11) | Number of the document | 2349287 |
| (13) | Kind of document | T |
| (96) | European patent application number | 09788170.0 |
| Date of filing the European patent application | 2009-03-11 | |
| (97) | Date of publication of the European application | 2011-08-03 |
| (45) | Date of publication and mention of the grant of the patent | 2018-08-15 |
| (46) | Date of publication of the claims translation |
| (86) | Number | PCT/NL2009/050113 |
| Date | 2009-03-11 |
| (87) | Number | WO 2010/050802 |
| Date | 2010-05-06 |
| (30) | Number | Date | Country code |
| PCT/NL2008/0506 | 2008-10-27 | WO |
| (72) |
DE KIMPE, Josephus Johannes, NL
PLATENBURG, Gerardus Johannes, NL
VAN DEUTEKOM, Judith Christina Theodora, NL
AARTSMA-RUS, Annemieke, NL
VAN OMMEN, Garrit-Jan Boudewijn, NL
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| (73) |
Academisch Ziekenhuis Leiden,
Albinusdreef 2, 2333 ZA Leiden,
NL
BioMarin Technologies B.V., J.H. Oortweg 21, 2333 CH Leiden, NL |
| (54) | METHODS AND MEANS FOR EFFICIENT SKIPPING OF AT LEAST ONE OF THE FOLLOWING EXONS OF THE HUMAN DUCHENNE MUSCULAR DYSTROPHY GENE: 43, 46, 50- 53. |
| METHODS AND MEANS FOR EFFICIENT SKIPPING OF AT LEAST ONE OF THE FOLLOWING EXONS OF THE HUMAN DUCHENNE MUSCULAR DYSTROPHY GENE: 43, 46, 50- 53. |