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LT - METHODS AND MEANS FOR EFFICIENT SKIPPING OF AT LEAST ONE OF THE FOLLOWING EXONS OF THE HUMAN DUCHENNE MUSCULAR DYSTROPHY GENE: 43, 46, 50- 53.
EN - METHODS AND MEANS FOR EFFICIENT SKIPPING OF AT LEAST ONE OF THE FOLLOWING EXONS OF THE HUMAN DUCHENNE MUSCULAR DYSTROPHY GENE: 43, 46, 50- 53.

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Bibliographic data
Indications of the International Patent Classification (IPC)
(51) INT.CL. A61K 31/7105
C12N 5/10
A61K 48/00
A61P 21/00
European patent
(11) Number of the document 2349287
(13) Kind of document T
(96) European patent application number 09788170.0
Date of filing the European patent application 2009-03-11
(97) Date of publication of the European application 2011-08-03
(45) Date of publication and mention of the grant of the patent 2018-08-15
(46) Date of publication of the claims translation
PCT application
(86) Number PCT/NL2009/050113
Date 2009-03-11
PCT application publication
(87) Number WO 2010/050802
Date 2010-05-06
Priority applications
(30) Number Date Country code
PCT/NL2008/0506 2008-10-27 WO
Inventors
(72)
DE KIMPE, Josephus Johannes, NL
PLATENBURG, Gerardus Johannes, NL
VAN DEUTEKOM, Judith Christina Theodora, NL
AARTSMA-RUS, Annemieke, NL
VAN OMMEN, Garrit-Jan Boudewijn, NL
Grantee
(73) Academisch Ziekenhuis Leiden, Albinusdreef 2, 2333 ZA Leiden, NL
BioMarin Technologies B.V., J.H. Oortweg 21, 2333 CH Leiden, NL
Title
(54) METHODS AND MEANS FOR EFFICIENT SKIPPING OF AT LEAST ONE OF THE FOLLOWING EXONS OF THE HUMAN DUCHENNE MUSCULAR DYSTROPHY GENE: 43, 46, 50- 53.
  METHODS AND MEANS FOR EFFICIENT SKIPPING OF AT LEAST ONE OF THE FOLLOWING EXONS OF THE HUMAN DUCHENNE MUSCULAR DYSTROPHY GENE: 43, 46, 50- 53.