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Teisinis statusas
Patentas neįsigaliojo (pagal EPK)
(51) | INT.CL. | A61K 31/7105 | |
C12N 5/10 | |||
A61K 48/00 | |||
A61P 21/00 |
(11) | Patento numeris | 2349287 |
(13) | Dokumento rūšis | T |
(96) | Europos patento paraiškos numeris | 09788170.0 |
Europos patento paraiškos padavimo data | 2009-03-11 | |
(97) | Europos patento paraiškos paskelbimo data | 2011-08-03 |
(45) | Paskelbimo apie Europos patento išdavimą data | 2018-08-15 |
(46) | Apibrėžties vertimo paskelbimo data |
(86) | Numeris | PCT/NL2009/050113 |
Data | 2009-03-11 |
(87) | Numeris | WO 2010/050802 |
Data | 2010-05-06 |
(30) | Numeris | Data | Šalis |
PCT/NL2008/0506 | 2008-10-27 | WO |
(72) |
DE KIMPE, Josephus Johannes, NL
PLATENBURG, Gerardus Johannes, NL
VAN DEUTEKOM, Judith Christina Theodora, NL
AARTSMA-RUS, Annemieke, NL
VAN OMMEN, Garrit-Jan Boudewijn, NL
|
(73) |
Academisch Ziekenhuis Leiden,
Albinusdreef 2, 2333 ZA Leiden,
NL
BioMarin Technologies B.V., J.H. Oortweg 21, 2333 CH Leiden, NL |
(54) | METHODS AND MEANS FOR EFFICIENT SKIPPING OF AT LEAST ONE OF THE FOLLOWING EXONS OF THE HUMAN DUCHENNE MUSCULAR DYSTROPHY GENE: 43, 46, 50- 53. |
METHODS AND MEANS FOR EFFICIENT SKIPPING OF AT LEAST ONE OF THE FOLLOWING EXONS OF THE HUMAN DUCHENNE MUSCULAR DYSTROPHY GENE: 43, 46, 50- 53. |